In the Gene and Advanced Therapies: Creating Value in the Patient Journey and in the Health System Forum, held by the Syndicate of the Pharmaceutical Industries (Sindusfarma) and the National Health Surveillance Agency (Anvisa) on October 23 and 24, 2019, in the agency’s auditorium in Brasilia, public managers, physicians, national and international researchers, congressmen, and healthcare leaders shared experiences in Brazil and in other countries. They discussed various aspects related to the theme, such as regulation, clinical research, diagnosis, legislation, financing, and sustainability of the system.